Small functional changes in people with progressive muscle loss and encouraging preclinical findings are not equivalent to clear muscle gains in broader clinical populations
Trends In FDA FY2022 Inspection-based Warning Letters By Liz Oestreich, Madeleine Giaquinto, and Kalah Auchincloss The COVID-19 pandemic continued to impact FDAs inspection activities in FY2022 despite efforts to shift more of the agencys focus beyond the public health emergency
Gu S, Wang X, Qiao Q, Gao W, Wang J, Dong H
Efinopegdutide has been granted fast track designation by the FDA for the treatment of MASH (NCT04944992, NCT05877547) and this is the indication that the clinical development programme of this molecule will focus
The combination group showed 1.3 kg greater fat mass reduction measured via DEXA scan, though the difference did not reach statistical significance (p=0.08)
MeiraGTx Sector: Gene therapy and genetic medicines HQ: 655 Third Avenue, New York, NY Year Founded: 2016 Key Leaders: Alexandria Forbes, PhD, serves as President, CEO, and member of the Board of Directors Number of Employees: 350-400 Stage: Public Financial Snapshot: Market cap estimated between $744.94 million Notable Investors: Perceptive Advisors LLC, Sanofi, Johnson & Johnson, Adage Capital Partners Gp, LLC, Prosight Management, LP, Rubric Capital Management LP, BlackRock, Inc., 683 Capital Management, LLC, Millennium Management LLC, and J